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Platform Technology Designation Program for Drug Development

DraftCenter for Drug Evaluation and Research Center for Biologics Evaluation and Research05/28/2024

Description

This guidance provides details about the implementation of the platform technology designation program established by section 506K of the Federal Food, Drug, and Cosmetic Act (FD&C Act). This guidance outlines eligibility factors for receiving a platform technology designation, potential benefits of receiving a designation, how to leverage data from designated platform technologies, how to discuss a planned designation request as part of a milestone meeting, the recommended content of a designation request submission, and the review timelines for a designation request. This program is intended to result in efficiencies in drug development, manufacturing, and review processes for drug product applications that incorporate designated platform technologies.

Scope & Applicability

Product Classes

5
Combination Product

Products combining drug, device, or biological constituents; Generally recommended for Enhanced Documentation; Requires 14971-based framework incorporating ICH Q9; A drug-device combination where the device constituent part detects ingestion.

Biological Product

Regulated under section 351(i) of the PHS Act; Virus, therapeutic serum, toxin, vaccine, or protein applicable to prevention or treatment; Alternative regulation category for products meeting device definition

mRNA Vaccine

Example of a potential platform technology

Gene Therapy

A type of ATMP involving recombinant nucleic acids or viral vectors.

Monoclonal Antibody

Anti-TNF-alpha drug substance and drug product

Stakeholders

2
Sponsor

Entity responsible for submitting applications under section 524B

BLA holder

Entity expected to have control over manufacturing for biological products

Regulatory Context

Attributes

3
Significant Efficiencies

Eligibility factor for platform technology designation

Designated Platform Technology

Status granted to technologies meeting eligibility factors

Preliminary Evidence

Information from completed tests or studies to support designation

Identified Hazards

Hazards

1
Adverse effect on quality

Risk to be evaluated when adapting platform technology

Related CFR Sections (4)

See Also (8)

Platform Technology Designation Program for Drug Development | Guideline Explorer | BioRegHub