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Considerations for Plasmid DNA Vaccines for Infectious Disease Indications: Guidance for Industry

FinalCenter for Biologics Evaluation and Research11/01/2007

Description

This guidance describes our current recommendations concerning preclinical development and testing of DNA vaccines to prevent infectious diseases. This guidance supercedes the 1996 Points to Consider document. In addition, this guidance finalizes the draft guidance of the same title dated February 2005.

Scope & Applicability

Product Classes

2
Plasmid DNA Vaccines

purified plasmid preparations containing one or more DNA sequences capable of inducing and/or promoting an immune response against a pathogen; Primary product class discussed in the guidance

DNA vaccine

Nucleic-acid based vaccines

Regulatory Context

Attributes

1
residual moisture

test performed if the plasmid product is lyophilized

Identified Hazards

Hazards

4
Adventitious agent contamination

Potential risk in the manufacturing of cell therapy products.

Genomic integration

Potential risk of plasmid DNA vaccines after injection

autoimmunity

potential adverse consequence of immunomodulatory genes

tumorigenisis

theoretical risk associated with DNA integration

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