Back to Explorer

CVM GFI #204 Active Controls in Studies to Demonstrate Effectiveness of a New Animal Drug for use in Companion Animals

FinalCenter for Veterinary Medicine12/01/2015

Description

This guidance document advises industry on the use of active controls in studies intended to provide substantial evidence of effectiveness to support product approval for new animal drugs used in cats, dogs, and horses (i.e., companion animals). This guidance document is directed at clinical investigators who conduct studies using active controls and have a basic understanding of statistical principles. In this document, CVM compares studies that use active controls to studies that use either placebo concurrent controls or untreated concurrent controls. CVM uses these comparisons to illustrate the appropriate use of an active control.

Scope & Applicability

Product Classes

3
New Animal Drug

The category of products covered by this guidance.

Active Control

A drug whose effect is well-defined and used as a comparator in NI trials; drug used as a comparator in a non-inferiority trial; A drug with known effectiveness used as a comparator in an NI trial.; Used in trials where a placebo is not ethical or feasible.

Placebo Control

Inactive substance used as a comparator to establish effectiveness

Stakeholders

4
Clinical investigators

Source of safety information in clinical trials

Applicant

Entity submitting development data and knowledge; Entity performing the work process for change

Animal Owner

Role of the person who may have administered the VMP

Committee for Medicinal Products for Human Use

CHMP within the European Medicines Agency

Regulatory Context

Attributes

5
Margin of difference

Symbolized as Delta (Δ), defines the extent a drug can be less effective and still be non-inferior

Assay sensitivity

Ability of a study to detect the study endpoint of interest

Inferential value

The ability to make inferences from study results to the overall target population

Sample Size

statistically justified calculation required in the plan

Randomization Ratio

The ratio of subjects allocated to control versus drug arms, which may change over time.

Related CFR Sections (2)

See Also (2)

CVM GFI #204 Active Controls in Studies to Demonstrate Effectiveness of a New Animal Drug for use in Companion Animals | Guideline Explorer | BioRegHub