Back to Explorer

COVID-19: Developing Drugs and Biological Products for Treatment or Prevention: Guidance for Industry

FinalCenter for Biologics Evaluation and Research Center for Drug Evaluation and Research11/24/2023

Description

The Food and Drug Administration (FDA or Agency) is announcing the availability of a final guidance for industry entitled “COVID-19:  Developing Drugs and Biological Products for Treatment or Prevention.”  The purpose of this guidance is to assist sponsors in the clinical development of drugs and biological products for the treatment or prevention of COVID-19.  This guidance describes FDA’s current recommendations for phase 2 and phase 3 trials with a focus on trial population, trial design, efficacy endpoints, safety considerations, and statistical considerations.  This guidance supersedes the guidance of the same name initially issued on May 19, 2020, and reissued on February 22, 2021.

Scope & Applicability

Product Classes

4
Biological Product

Regulated under section 351(i) of the PHS Act; Virus, therapeutic serum, toxin, vaccine, or protein applicable to prevention or treatment; Alternative regulation category for products meeting device definition

Investigational drug

drug where there has been no prior determination of safety or effectiveness

Gene Therapy

A type of ATMP involving recombinant nucleic acids or viral vectors.

Cellular Therapy

Additional considerations may exist for cellular therapies.

Stakeholders

5
Sponsor

Entity responsible for submitting applications under section 524B

Sponsors

Assist sponsors in the nonclinical evaluation

Division of Antiviral Products

FDA division receiving next generation sequencing data

DMC

Data monitoring committee; Oversight body that may request interim analysis

Data Monitoring Committee

Safety oversight body for interpreting adverse events; Safety oversight body for study design

Regulatory Context

Attributes

5
Serious adverse events

Streamlined safety data collection category

SpO2

The displayed oxygen saturation value which may have a range of uncertainty.; pulse oximeter oxygen saturation measurement; Functional oxygen saturation measured by the device; estimated oxygen level reading

Baseline Severity

FDA recommends sponsors categorize the baseline severity of COVID-19.

EC50

determine the neutralizing activity (half maximal effective concentration (EC50) value)

EC90

Antiviral activity measurement against variants

Related CFR Sections (2)

Related Warning Letters (10)

  • Clinical Investigator

    Shirish M. Gadgeel, M.D.

    2025-09-09
  • Clinical Investigator

    Mark J. Savant, M.D

    2025-07-15
  • Bioresearch Monitoring Program/Institutional Review Board (IRB)

    United Health Products, Inc.

    2025-05-20
  • Clinical Investigator

    Americo F. Padilla, M.D.

    2025-03-25
  • Institutional Review Board (IRB)

    Armstrong County Memorial Hospital

    2024-11-05
  • Clinical Investigator

    Namita A. Goyal, M.D.

    2024-10-22
  • Institutional Review Board (IRB)

    Louisiana State University Health Science Center IRB

    2024-10-08
  • Bioresearch Monitoring Program/IRB

    Massachusetts Institute of Technology MIT

    2024-07-16
  • Institutional Review Board (IRB)

    New York State Psychiatric Institute IRB

    2024-03-26
  • Investigational Device Exemptions (Clinical Investigator)

    Mobeen Mazhar, M.D.

    2023-06-06

See Also (8)