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Requesting FDA Feedback on Combination Products : Guidance for Industry and FDA Staff

FinalOffice of the Commissioner,Office of Clinical Policy and Programs,Office of Combination Products Center for Biologics Evaluation and Research Center for Drug Evaluation and Research Center for Devices and Radiological Health12/04/2020
CGMPCGMPsPharmaceutical Quality/Chemistry and Manufacturing ControlsHuman Factors

Description

The purpose of this guidance is to discuss ways in which combination product sponsors  can obtain feedback from FDA on scientific and regulatory questions and to describe best practices for FDA and sponsors when interacting on these topics.  These interactions can occur through application-based mechanisms, such as the pre-submission process used in the Center for Devices and Radiological Health (CDRH) and the Center for Biologics Evaluation and Research (CBER)  and the formal meetings used in the Center for Drug Evaluation and Research (CDER) and CBER,  or through Combination Product Agreement Meetings (CPAMs),  as appropriate.

Key Topics

Terms and concepts identified from this document

Scope & Applicability

Product Classes

3
Combination Product

Products combining drug, device, or biological constituents; Generally recommended for Enhanced Documentation; Requires 14971-based framework incorporating ICH Q9; A drug-device combination where the device constituent part detects ingestion.

Regenerative Medicine Advanced Therapy

Products granted RMAT designation status.

Breakthrough Device

Devices providing for more effective treatment or diagnosis of life-threatening diseases

Stakeholders

5
Sponsor

Entity responsible for submitting applications under section 524B

Product Jurisdiction Officer

FDA official consulted for device definition or center assignment issues.; Official consulted for jurisdictional determinations.; Official determining center assignment

Point of Contact

Single individual designated to represent the OTC IWG in communications with FDA.

POC

FDA Point of Contact for meeting coordination.

OCP

Office of Combination Products, assists in resolving regulatory issues.

Regulatory Context

Regulatory Activities

10
CPAM

Combination Product Agreement Meetings established by the Cures Act; Combination Product Agreement Management

Pre-submission

Mechanism to request FDA feedback on planned modeling activities.

Special Protocol Assessment

repeat-dose toxicity studies that support a carcinogenicity Special Protocol Assessment (SPA)

Abbreviated New Drug Application

ANDA submission containing a waiver request

Biologic License Application

BLA under section 351(a) or 351(k)

New Drug Application

Rule does not apply to products marketed under an NDA

Investigational New Drug Application

IND for treatment use; Regulatory submission required for clinical trials and expanded access.

Premarket Notification

A medical device submission type (510(k)).

Premarket Approval Application

Marketing submission type requiring QMS information; Type of marketing submission requiring QMS information

IND

Investigational New Drug submissions

Document Types

3
Master File

Documentation artifact related to NDI notifications

eCTD Specifications

Electronic Common Technical Document format for submissions.

eCopy

The required electronic format for submissions to the FDA.

Attributes

1
Primary Mode of Action

Single mode of action expected to make the greatest contribution to therapeutic effects

Technical Details

Testing Methods

1
Study Design

scientific issues appropriate for application-based mechanisms

Processes

1
CMC

chemistry, manufacturing, and controls

Standards & References

External Standards

2
PHS Act

Public Health Service Act, specifically section 402(j)(1)(A)(ii) regarding clinical trials.

Public Health Service Act

Licensing of biological products

Related CFR Sections (1)

Related MFDS Guidelines

Korean regulatory guidelines covering similar topics

See Also (8)

Requesting FDA Feedback on Combination Products : Guidance for Industry and FDA Staff | Guideline Explorer | BioRegHub