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Providing Postmarket Periodic Safety Reports in the ICH E2C(R2) Format (Periodic Benefit-Risk Evaluation Report)

FinalCenter for Biologics Evaluation and Research Center for Drug Evaluation and Research11/29/2016

Description

This guidance describes the conditions under which applicants can use an alternative reporting format, the International Council for Harmonisation (ICH)3 E2C(R2) Periodic Benefit-Risk Evaluation Report (PBRER), in place of the U.S. periodic adverse drug experience report (PADER), U.S. periodic adverse experience report (PAER), or ICH E2C Periodic Safety Update Report (PSUR), to satisfy the periodic postmarketing safety reporting requirements in §§ 314.80(c)(2) and 600.80(c)(2) (21 CFR 314.80(c)(2) and 600.80(c)(2)). This guidance also describes the procedures applicants should follow if they wish to submit a PBRER in place of a PADER, PAER, or PSUR. The steps will differ, depending on whether or not the applicant has an approved waiver in place to substitute the PSUR for the PADER/PAER.

Key Topics

Terms and concepts identified from this document

Scope & Applicability

Stakeholders

1
applicant

entity submitting marketing applications

Regulatory Context

Regulatory Activities

5
eCTD

Electronic Common Technical Document format for submissions; Electronic Common Technical Document specifications; Electronic Common Technical Document submission format; Electronic Common Technical Document specifications for submissions

Waiver Request

Request to waive regulatory requirements under 314.99(b).

BLA

Biologics License Application

ANDA

Abbreviated New Drug Application

NDA

New Drug Application

Document Types

5
ICSR

Individual Case Safety Report

PSUR

Periodic Safety Update Report

PAER

U.S. periodic adverse experience report; Periodic Adverse Experience Report

PADER

U.S. periodic adverse drug experience report; Periodic Adverse Drug Experience Report

PBRER

Periodic Benefit-Risk Evaluation Report; Periodic Benefit-Risk Evaluation Report used for safety reporting.; Periodic Benefit-Risk Evaluation Report used for benefit-risk assessment

Attributes

2
Data Lock Point

The date designated as the cut-off for data to be included in the report

DLP

Data Lock Point for the PBRER

Technical Details

Substances

1
Active Moiety

Basis for determining drug sameness

Clinical Concepts

1
adverse drug experience

description of an event related to an individual patient or subject

ICH References (2)

ICH E2C(R1)

Source of the definition for Spontaneous Reporting

ICH E2C(R2)

Periodic Benefit-Risk Evaluation Report (PBRER) standard for marketed products; Periodic Benefit-Risk Evaluation Report guidance; The primary guidance document for Periodic Benefit-Risk Evaluation Reports.; Periodic Benefit-Risk Evaluation Report (PBRER) guidance

Related CFR Sections (5)

Related MFDS Guidelines

Korean regulatory guidelines covering similar topics

See Also (8)

Providing Postmarket Periodic Safety Reports in the ICH E2C(R2) Format (Periodic Benefit-Risk Evaluation Report) | Guideline Explorer | BioRegHub