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Q12 Technical and Regulatory Considerations for Pharmaceutical Product Lifecycle Management Guidance for Industry: Guidance for Industry

FinalCenter for Drug Evaluation and Research Center for Biologics Evaluation and Research05/11/2021
Pharmaceutical Quality SystemProcess ValidationQuality Risk ManagementCAPAChange ManagementPQSGMP complianceGood Manufacturing PracticesControl StrategyCritical Process ParametersData Integrity

Description

This guidance provides a framework to facilitate the management of postapproval chemistry, manufacturing, and controls (CMC) changes in a more predictable and efficient manner. A harmonized approach regarding technical and regulatory considerations for lifecycle management will benefit patients, industry, and regulatory authorities by promoting innovation and continual improvement in the pharmaceutical sector, strengthening quality assurance, and improving supply of medicinal products.

Key Topics

Terms and concepts identified from this document

Scope & Applicability

Product Classes

3
Combination Product

Products combining drug, device, or biological constituents; Generally recommended for Enhanced Documentation; Requires 14971-based framework incorporating ICH Q9; A drug-device combination where the device constituent part detects ingestion.

Biological Product

Regulated under section 351(i) of the PHS Act; Virus, therapeutic serum, toxin, vaccine, or protein applicable to prevention or treatment; Alternative regulation category for products meeting device definition

Drug-Device Combination Products

Products for which ECs must be defined for device elements.

Stakeholders

5
Regulatory Authorities

Early discussion is recommended regarding safety dataset size.; Entities with whom the adequacy of RWD and extrapolation plans should be discussed.; early discussion useful when proposed endpoints differ; Entities that should agree upon success criteria in advance.

Quality Unit

Oversees reprocess or rework of batches

Quality Affairs Personnel

Stakeholders involved in change control process

Marketing Authorization Holder

Entity responsible for managing the submission of PBRERs

MAH

Marketing Authorization Holder responsible for safety reporting; Marketing Authorization Holder responsible for providing exposure data; Marketing Authorization Holder responsible for signal evaluation and reporting.; Marketing Authorization Holder responsible for presenting efficacy information

Regulatory Context

Regulatory Activities

6
MAA

Marketing Authorization Application referenced for submission of ECs and PACMPs.

Inspection

FDA verification of qualified facility status, including for-cause inspections

PACMP

Post-Approval Change Management Protocol examples; Postapproval Change Management Protocol; Post-Approval Change Management Protocol for site transfers and process changes

Marketing Application

Submission for product approval

Postapproval Change Management Protocol

Regulatory tool providing predictability for future CMC changes

Marketing Authorization Application

Submissions supported by clinical trial data.

Document Types

10
Postapproval Change Management Protocol

PACMP used as a tool for life cycle management

Quality Agreement

Written agreements with suppliers of goods and services to ensure compliance with CGMP.

Product Quality Review

ensures that the change is included and assessed as part of the PQR

PLCM document

Product Lifecycle Management document outlines the specific plan for product lifecycle management.

CTD Module 3.2.R

Location where the PACMP document can be located.; The PLCM document can be located in CTD Module 3.2.R.

Active Substance Master File

Referenced submission in an MAA.

Type II Drug Master File

OPQ reviews controlled correspondence inquiries related to Type II drug master files

Product Lifecycle Management Document

Document outlining ECs and reporting categories; PLCM document included in eCTD section 3.2.R; Document including proposed ECs and reporting categories; Appendix C example of a PLM document

Common Technical Document

Format for submitting development information; Module 3 of the CTD for detailed descriptions of analytical procedures; ICH guideline M4Q(R1) for the registration of pharmaceuticals.

Marketing Authorization Application

Submissions to the MAA regarding postapproval changes

Attributes

5
Reporting Category

Classification of CMC changes based on risk to product quality; Classification for making changes to approved ECs.

Critical Quality Attribute

The degree of uncertainty can impact the critical quality attribute (CQA) risk ranking

Critical Process Parameter

CPPs that can influence CQAs

Shelf Life

Determined based on stability data; Established through stability testing; also called dating period.; Established through formal stability studies; Establishing the period during which a drug product is expected to remain within specifications; Period for drug products; The period during which a drug product is expected to remain within specifications; Duration product remains within acceptance criteria; Period during which product remains within specifications; Established for intermediates pu

Material Attributes

Process inputs used to describe the design space.; measured material attributes used in real time release testing

Technical Details

Substances

3
Drug Substance

Postapproval changes to drug substances; the active pharmaceutical ingredient being modified; Evaluation of physical properties for drug substance; Active ingredient intended to furnish pharmacological activity; The molecule or ion responsible for the physiological or pharmacological action.; The active pharmaceutical ingredient subject to postapproval changes

Excipient

Component used in human and animal drugs

Drug Product

Finished dosage form undergoing stability testing

Testing Methods

8
Stability Data Approaches

Used to support the evaluation of CMC changes

Analytical Procedure

The analytical procedure refers to the way of performing the analysis.

Stability Studies

Long-term, accelerated, and forced degradation studies to ensure shelf life.; studies to be performed to demonstrate suitability

Batch release

Tests performed to evaluate the potential impact of proposed changes.

Stability

Tests performed to evaluate the potential impact of proposed changes.

Confirmatory Stability Studies

Used to enable timely implementation of CMC changes

Analytical Procedures

Used to examine samples for physical, chemical or biological changes

Process Analytical Technology

PAT is used to monitor conversion and measure impurities.

Processes

4
CMC Changes

Categorization of postapproval Chemistry, Manufacturing, and Controls changes

Process qualification

Steps to be completed before implementation of a change.

Chemistry, Manufacturing, and Controls

Development program considerations for EUA

Manufacturing Process

Changes to this process may affect the identity and NDI status of an ingredient.; Changes to this process may create an NDI; you should describe the manufacturing process and provide detailed information; includes fermentation as an intrinsic part of identity

Standards & References

External Standards

1
Pharmacopoeial Monographs

Changes to comply with new monographs are out of scope

Specifications

2
Finished Product Specifications

Part of the control strategy to assure product quality.

Acceptance criteria

Metrics established by developers for each test element.

ICH References (10)

ICH Q12

Technical and Regulatory Considerations for Pharmaceutical Product Lifecycle Management; referenced for established conditions and life cycle management tools; in line with recommendations described in ICH Q12; Guideline for technical and regulatory considerations for pharmaceutical product lifecycle management; Technical and Regulatory Considerations for Pharmaceutical Product Lifecycle Management.

ICH Q8

Principles of Quality by Design described within ICH Q8-Q11.; Pharmaceutical development guidance; Pharmaceutical development and CQA measurement during processing; Defines product lifecycle phases; Referenced for Critical Quality Attributes (CQA); Pharmaceutical Development.; General principles related to model development, validation and verification; Principles described in ICH Q8 apply to stability models; Pharmaceutical Development guideline mentioned regarding enhanced level of understandi

ICH Q5E

Comparability of Biotechnological/Biological Products Subject to Changes in Their Manufacturing Process

ICH Q2(R1)

Validation of Analytical Procedures: Text and Methodology

ICH M4

Organization of the Common Technical Document; Organization of the Common Technical Document for the Registration of Pharmaceuticals for Human Use

ICH Q1A(R2)

Stability Testing of New Drug Substances and Products

ICH Q8(R2)

Pharmaceutical Development

ICH Q9

Quality Risk Management recommended for combination products

ICH Q10

Pharmaceutical Quality System

ICH Q11

Development and Manufacture of Drug Substances; General principles for selection of starting materials

Related CFR Sections (3)

Enforcement Impact

Deficiencies cited in Warning Letters referencing the same regulations

Quality control unit failed to exercise its responsibility
101
Failure to conduct at least one test to verify the identity of each component
95
Failure to establish adequate written procedures for production and process control
88
Failure to have appropriate laboratory determination of satisfactory conformance to final specifications
56
Failure to thoroughly investigate any unexplained discrepancy or failure of a batch
56
Failure to establish an adequate quality control unit
49
Failure to test samples of each component for identity and conformity
47
Failure to establish laboratory controls
35
Failure to thoroughly investigate any unexplained discrepancy
28
Failure to test samples of each component for identity
25

Related Warning Letters (10)

Related MFDS Guidelines

Korean regulatory guidelines covering similar topics

See Also (8)