Back to Explorer

E3 Structure and Content of Clinical Study Reports - Questions and Answers (R1)

FinalCenter for Drug Evaluation and Research Center for Biologics Evaluation and Research01/29/2013
Protocol DeviationGood Clinical Practice

Description

Since the ICH E3 guidance was made final, experiences implementing the guidance in the ICH regions have given rise to requests for clarification. This question and answer (Q&A) document is intended to facilitate implementing the ICH E3 guidance by clarifying key issues.

Key Topics

Terms and concepts identified from this document

Scope & Applicability

Product Classes

2
Stem Cells

Product category requiring specific CSR data

Gene Therapy

A type of ATMP involving recombinant nucleic acids or viral vectors.

Stakeholders

4
Patient

Way questions are framed is critical to collecting unbiased patient input

Ethics Committee

Clear understanding for ethics committees and regulators.

Investigator

Responsible for qualifications, training, and trial conduct; Individual responsible for trial conduct and data governance at a site.; May delegate tasks but retains overall responsibility; Person responsible for the conduct of the clinical trial at a trial site; Responsible for trial conduct and participant safety; Responsible for trial conduct, data integrity, and investigational product management.; Individual responsible for trial conduct at a site and informing the institution.; maintaining

sponsor

responsible for justifying omission of studies

Regulatory Context

Regulatory Activities

1
Marketing Application

Submission for product approval

Document Types

10
Disposition Flowchart

Example flowchart showing the disposition of patients in a clinical study.

Study Tagging File

STF used in eCTD v3.2.2 to reference datasets

Electronic Common Technical Document

eCTD specifications for regulatory submissions

Audit Certificate

provided by the sponsor when required by regulatory requirements

Case Report Form

collect on the case report form (CRF) the Investigator's clinical interpretation

Protocol

Defines the standard of veterinary practice and limits for anesthetic regimens

Trial Master File

Repositories held by the sponsor for essential records

Synopsis

Brief summary format for exploratory genomic data.

Common Technical Document

Format for submitting development information; Module 3 of the CTD for detailed descriptions of analytical procedures; ICH guideline M4Q(R1) for the registration of pharmaceuticals.

Clinical Study Report

CSR supported by ADaM datasets; Contains analysis results and animal listings

Attributes

3
Drug-Relatedness

Causality assessment of adverse events

Treatment Compliance

Adherence to study drug regimen

demographic baseline information

ICH E3 suggests presentation of this information in the efficacy evaluation

Technical Details

Testing Methods

2
Statistical Methods

Analysis of test data and rationale for sample sizes

Assay Validation

Verification of analytical procedures

Processes

1
pharmacokinetic studies

studies for which ICH E3 was not originally designed but can be adapted

Clinical Concepts

9
Double-Blinded Medication

Patients receiving double-blinded medication in the study regimen.

Efficacy

Unsatisfactory response regarding efficacy as a reason for withdrawal.

Important Protocol Deviation

Deviation affecting data reliability or subject safety

Protocol Deviation

Departure from study design or procedures

Serious Adverse Event

Adverse events resulting in death, hospitalization, or significant disability.

Adverse Event

Reactions or events observed in patients; Information described in an ICSR; Information associated with the use of biopharmaceuticals; Clinical information corrected during an amendment; Section D describes the singular subject who experienced one or several adverse events/reactions.; Reactions or events observed in patients or foetuses; The onset of a reaction/event following drug administration.; Reporting of reactions to suspect drugs; Reaction or event reported by the primary source; Reactio

open-label safety studies

basic principles can be applied to these trials

clinical pharmacology studies

basic principles can be applied to these trials

adequate and well-controlled clinical effectiveness studies

ICH E3 was developed for submission of these studies

Standards & References

Specifications

1
quality of life outcomes

studies with health economic or quality of life outcomes

ICH References (4)

ICH E6

Referenced for safety data collection and adverse event reporting plans.

ICH M4E

Evaluation of benefit/risk across regions or important subpopulations

ICH M4

Organization of the Common Technical Document; Organization of the Common Technical Document for the Registration of Pharmaceuticals for Human Use

ICH E3

document remedial actions in the clinical trial report; Structure and Content of Clinical Study Reports standards.

Related MFDS Guidelines

Korean regulatory guidelines covering similar topics

See Also (8)

E3 Structure and Content of Clinical Study Reports - Questions and Answers (R1) | Guideline Explorer | BioRegHub